Treating rare diseases: the challenge of orphan drugs
Orphan drugs are drugs used to treat rare diseases. In April 2025, NICE adopted new criteria for evaluating drugs for 'ultra rare' diseases.
No abstract for this publication.
Publication type:
policy brief
Publication language:
English
Publication date:
2025-07
Publication URL:
https://doi.org/10.58248/RR83
Institute:
Parliamentary Office of Science and Technology of the UK Parliament (POST)
Country:
United Kingdom of Great Britain & Northern Ireland

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